Health-related quality of life in patients living with Wilson disease in Spain: a cross-sectional observational study
Cross-sectional observational study conducted in patients diagnosed of Wilson disease. The results of the study show a high proportion of patients with impairment mainly in the emotional domain. Although many patients are satisfied with the treatment, they feel that they have to take too many tablets daily, which could affect adherence. The study indicates that […]
Changing Landscape of Orphan Drug Reimbursement – Evidence From EU-4 and England
Germany continuously provides the most robust patient access to ODs, wide access to ODs is maintained in France despite an increased percentage of ODs still in the price negotiation due to the Early Access programme. The largest improvement can be seen in Italy which corresponds to the legislative changes in the pricing negotiation process and […]
The view of experts on initiatives to be undertaken to promote equityin the access to orphan drugs and specialised care for rare diseases inSpain: A Delphi consensus
Experts consensus on the future of rare diseases care and orphan drugs access in Spain: a Delphi study
Experts consensus on actions for enhancing healthcare and access to orphan drugs in Spain.
